The Next Generation of Rare Disease Drug Policy

April 7, 2022

The United States defines a rare disease as a condition affecting fewer than 200,000 people in the
country or one in which “there is no reasonable expectation” of recovering research and
development costs.1 Examples of rare diseases include genetically-linked cancers, cystic fibrosis,
and debilitating pediatric conditions like Gaucher disease and spinal muscular atrophy

Spotlight

Celon Laboratories Limited

Celon Labs is a leader in the development and marketing of specialty products which serve niche therapy areas. Using in-house research & development capabilities, operational flexibility, manufacturing and regulatory expertise, Celon has taken a wide variety of products from laboratory to the market.

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whitePaper | November 18, 2022

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A pragmatic approach to developing rare disease drug

whitePaper | July 13, 2023

Most medicines in development today target diseases affecting large sections of the global population. But now we are slowly beginning to see a rise in the interest of developing ”orphan drugs,” or pharmaceutical agents intended to treat rare diseases.

The Never-Normal Future of Manufacturing

whitePaper | September 24, 2022

Let’s just say what we’re all thinking: 2020 was rough. It threw pretty much every element of our lives into disarray, and we suddenly had to become experts at navigating a new way of working, schooling and socializing.