Next Generation Therapies: Innovative Drug Development Approaches for Rare Diseases

December 26, 2018

Scientific interest in rare disease drug discovery has been growing exponentially and the number of new therapies targeting rare and orphan diseases has doubled in the past 6 years. In this white paper, we have reviewed innovative approaches to develop successful therapies for rare diseases such as gene replacement therapies, antisense oligos, and monoclonal antibodies. We also highlight some of the new classes of therapies including the epigenome and microbiome.

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Phoenix Healthcare LLC

Phoenix Healthcare provides a variety of products to Pharmaceutical companies including a choice of programs to resource candidates as well as specialist training support. These products are client focused and specifically designed to suit their business needs and offer institutional caliber service. Our mission is to provide our clients, regardless of size, institutional caliber service combined with innovative solutions to the challenges facing Companies within the Pharmaceutical, BioTech and Medical Device Industries.

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