Next Generation Therapies: Innovative Drug Development Approaches for Rare Diseases

December 26, 2018

Scientific interest in rare disease drug discovery has been growing exponentially and the number of new therapies targeting rare and orphan diseases has doubled in the past 6 years. In this white paper, we have reviewed innovative approaches to develop successful therapies for rare diseases such as gene replacement therapies, antisense oligos, and monoclonal antibodies. We also highlight some of the new classes of therapies including the epigenome and microbiome.

Spotlight

PHOENIX All-in-One

All-in-One: Our expertise and coverage for the success of manufacturer partners to provide manufacturer partners a unified approach to the European and all 26 local markets, the PHOENIX group has brought the service brand “All-in-One” into life. All-in-One grants a direct access for manufacturers to patients. With its eight focus areas from a Pan-European Preferred Partnerships, Healthcare Logistics, Business Intelligence, Patient Services to Supply Chain Optimization, Sales Support, Clinical Trial Supply Services and Services for Specialty Drugs, All-in-One has an unparalleled service to manufacturer partners throughout Europe. You do your core business – we care about the rest Our full-service offering enables manufacturers to focus on their core competencies – developing and successfully commercializing innovative products and solutions. We care about the rest. “All-in-One is more than just a collection of services, it is a unified approach to patients all over Europe”, says Stefan

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Spotlight

PHOENIX All-in-One

All-in-One: Our expertise and coverage for the success of manufacturer partners to provide manufacturer partners a unified approach to the European and all 26 local markets, the PHOENIX group has brought the service brand “All-in-One” into life. All-in-One grants a direct access for manufacturers to patients. With its eight focus areas from a Pan-European Preferred Partnerships, Healthcare Logistics, Business Intelligence, Patient Services to Supply Chain Optimization, Sales Support, Clinical Trial Supply Services and Services for Specialty Drugs, All-in-One has an unparalleled service to manufacturer partners throughout Europe. You do your core business – we care about the rest Our full-service offering enables manufacturers to focus on their core competencies – developing and successfully commercializing innovative products and solutions. We care about the rest. “All-in-One is more than just a collection of services, it is a unified approach to patients all over Europe”, says Stefan

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