The Powerful and Evolving Role of Patient Advocacy Groups in Orphan Drug Development

Premier Research

A major goal of patient advocacy groups is to address the unmet needs of patients with cancer or rare diseases by providing access to the most effective drugs. In recent years, patient advocacy groups have expanded their influence over the drug development continuum from discovery to approval to market entry. Many groups directly fund, help design, or recruit patients to participate in clinical trials.
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Spotlight

The aim of this hospital-based retrospective analysis is to estimate the prevalence of Lysosomal Storage Disease (LSDs) in the Eastern Province of Saudi Arabia between 1983 and 2016. A total number of 89 Saudi patients from 43 families were diagnosed with different types of LSDs within this time period.


OTHER ON-DEMAND WEBINARS

Pursuing Specialty Pharmacy: Understanding the Challenges and Benefits

Wolters Kluwer Clinical Drug Information

With nearly all healthcare organizations under pressure to cut costs and increase revenue, specialty pharmacy operations – when done correctly – present a shining light in the dark tunnel of budget cuts. Dr. Kyle Skiermont, director of specialty and infusion operations for Fairview Pharmacy Services in Minnesota, will discuss identifying specialty drugs, as well as tips potential barriers, and strategies for starting a specialty pharmacy business.
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Phenotypic Screening in Drug Discovery

Charles River Laboratories

In the past few years, there has been a revival of phenotypic screening for hit discovery and profiling. It is generally accepted that overexpression of targets in heterologous systems has a risk of creating functional artefacts, and in principle, such an assay is single-target focused.
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Oncology Drug Access Navigators - Benefits to Patients & Health Care Teams

Canadian Cancer Survivor Network

Alan Birch discussed the role of an Oncology Drug Access Navigator as well as how the role fits into the healthcare team and what they help patients with. He gave a brief overview and history of the role as well as discussing challenges faced by patients and how National Pharmacare may impact it all.
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Recent Technological Advancements in Medical Communication

Honeycomb Worldwide Inc

Join this webinar for a discussion of the most common medical communications business challenges and potential solutions. This event will also feature a live demonstration of how patient-centric medical communications technology can be leveraged to streamline and optimize medical inquiry fulfillment, adverse event reporting and product complaint management.
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Spotlight

The aim of this hospital-based retrospective analysis is to estimate the prevalence of Lysosomal Storage Disease (LSDs) in the Eastern Province of Saudi Arabia between 1983 and 2016. A total number of 89 Saudi patients from 43 families were diagnosed with different types of LSDs within this time period.

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