Who will be the biggest pharma players in orphan drugs?

New analysis from GlobalData has identified the predicted top 15 pharma players in 2025 for organ drugs, with Roche coming out in the lead. The research also notes that M&A deals have been the primary way in which big pharma companies secure these orphan drug designations, with very few rare disease drugs being developed in-house. “Despite the allure of the lucrative orphan drug market, this is not a viable sector for all pharma companies as it requires specialist capabilities,” GlobalData said. “In fact, most big pharma companies have inherited specialty business units through M&As.” The collective sales data from these therapies with organ drug designations reveal that Roche has generated the highest sales from orphan drugs and will maintain its leading position going forward.

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Business Wire | October 25, 2023

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PHARMA TECH

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Business Wire | October 05, 2023

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PHARMACY MARKET

Cytel continues expansion of market access and medical communication capabilities with the acquisition of co.faktor

Business Wire | September 28, 2023

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