Roches Hemlibra scores funding to treat much larger group of patients in England

FiercePharma | August 21, 2019

Roches Hemlibra has been storming out of the gate since its first approval in 2017. Now, its set to benefit a much wider patient group in England thanks to new funding from health authorities there. NHS England on Wednesday unveiled funding for Roches drug in hemophilia A patients without blood protein factor VIII inhibitors. Authorities last year approved the drug for people with the inhibitors, a much smaller group of patients. About 230 hemophilia A patients in England had inhibitors as of a 2015-2016 study, according to NHS England documents. The new development will allow about 2,000 patients to access the Roche drug, authorities said. Hemlibra is set to "change lives and lift a weight from thousands of parents," NHS chief executive Simon Stevens said in a statement. The hemophilia A med won its initial approval in Europe in February 2018 and in March 2019 scored approval to treat patients without inhibitors. Authorities in the U.S. approved the drug in November 2017.  Since it's been on the market, Hemlibra has been driving strong uptake and turning in big sales figures. During the first half of the year, the med turned in $545 million in global sales.

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ABI Research is a global technology intelligence firm delivering actionable research and strategic guidance to technology leaders, innovators, and decision-makers around the world.

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BUSINESS INSIGHTS, PHARMA TECH

KSQ Announces ONO’s Acquisition of Multiple Research-stage Oncology Programs

KSQ Therapeutics | January 30, 2023

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Ionis Pharma's Eplontersen for ATTRv-PN Gets FDA's NDA Acceptance

Ionis Pharmaceuticals, Inc. | March 10, 2023

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VERO Biotech Announces FDA Approval for Its Second-gen GENOSYL DS

VERO Biotech | February 03, 2023

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