Developing RNA Medicines for Rare Genetic Diseases

LAURA MASON | September 11, 2018

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There are approximately 7,000 known rare diseases, however, less than 6% of these have a treatment. It is estimated that between 25–35 million Americans live with a rare disease. The company ProQR is dedicated to developing new therapeutics for patients living with untreated rare diseases. We caught up with Daniel de Boer, Chief Executive Officer at ProQR to learn more about the company’s approach to finding new treatments for rare genetic diseases. 

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Genetics & Applications

Genetics and Applications (G&A) is the official journal of the Institute for Genetic Engineering and Biotechnology, University of Sarajevo. It is envisaged as an international journal issued twice a year in print and online format, publishing peer-reviewed articles of novel and significant discoveries in the fields of basic and applied genetics. Special issues or supplements may also be produced from time to time upon agreement with the Editorial Board.

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Spotlight

Genetics & Applications

Genetics and Applications (G&A) is the official journal of the Institute for Genetic Engineering and Biotechnology, University of Sarajevo. It is envisaged as an international journal issued twice a year in print and online format, publishing peer-reviewed articles of novel and significant discoveries in the fields of basic and applied genetics. Special issues or supplements may also be produced from time to time upon agreement with the Editorial Board.

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